Pulmonary endpoints in duchenne muscular dystrophy a workshop summary

Jonathan Finder, Oscar Henry Mayer, Daniel Sheehan, Hemant Sawnani, R. Ted Abresch, Joshua Benditt, David J. Birnkrant, Tina Duong, Erik Henricson, Kathi Kinnett, Craig M. McDonald, Anne M. Connolly

Research output: Contribution to journalArticle

20 Citations (Scopus)

Abstract

Development of novel therapeutics for treatment of Duchenne muscular dystrophy (DMD) has led to clinical trials that include pulmonary endpoints that allow assessment of respiratory muscle status, especially in nonambulatory subjects. Parent Project Muscular Dystrophy (PPMD) convened a workshop in Bethesda, Maryland, on April 14 and 15, 2016, to summarize published respiratory data in DMD and give guidance to clinical researchers assessing the effect of interventions on pulmonary outcomes in DMD.

Original languageEnglish (US)
Pages (from-to)512-519
Number of pages8
JournalAmerican Journal of Respiratory and Critical Care Medicine
Volume196
Issue number4
DOIs
StatePublished - Aug 15 2017

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Duchenne Muscular Dystrophy
Education
Lung
Respiratory Muscles
Muscular Dystrophies
Research Personnel
Clinical Trials
Therapeutics

All Science Journal Classification (ASJC) codes

  • Pulmonary and Respiratory Medicine
  • Critical Care and Intensive Care Medicine

Cite this

Finder, J., Mayer, O. H., Sheehan, D., Sawnani, H., Abresch, R. T., Benditt, J., ... Connolly, A. M. (2017). Pulmonary endpoints in duchenne muscular dystrophy a workshop summary. American Journal of Respiratory and Critical Care Medicine, 196(4), 512-519. https://doi.org/10.1164/rccm.201703-0507WS

Pulmonary endpoints in duchenne muscular dystrophy a workshop summary. / Finder, Jonathan; Mayer, Oscar Henry; Sheehan, Daniel; Sawnani, Hemant; Abresch, R. Ted; Benditt, Joshua; Birnkrant, David J.; Duong, Tina; Henricson, Erik; Kinnett, Kathi; McDonald, Craig M.; Connolly, Anne M.

In: American Journal of Respiratory and Critical Care Medicine, Vol. 196, No. 4, 15.08.2017, p. 512-519.

Research output: Contribution to journalArticle

Finder, J, Mayer, OH, Sheehan, D, Sawnani, H, Abresch, RT, Benditt, J, Birnkrant, DJ, Duong, T, Henricson, E, Kinnett, K, McDonald, CM & Connolly, AM 2017, 'Pulmonary endpoints in duchenne muscular dystrophy a workshop summary', American Journal of Respiratory and Critical Care Medicine, vol. 196, no. 4, pp. 512-519. https://doi.org/10.1164/rccm.201703-0507WS
Finder, Jonathan ; Mayer, Oscar Henry ; Sheehan, Daniel ; Sawnani, Hemant ; Abresch, R. Ted ; Benditt, Joshua ; Birnkrant, David J. ; Duong, Tina ; Henricson, Erik ; Kinnett, Kathi ; McDonald, Craig M. ; Connolly, Anne M. / Pulmonary endpoints in duchenne muscular dystrophy a workshop summary. In: American Journal of Respiratory and Critical Care Medicine. 2017 ; Vol. 196, No. 4. pp. 512-519.
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